-
Targeting (for) cheaper CAR-T therapies
Following a single dose of CAR-T therapy, cancer patients for whom all other treatment options have failed have gone into complete remission. Read More…
-
CRISPR/Cas9 editing of a giant gene: towards a new therapeutic frontier for Duchenne muscular dystrophy
The human genome contains approximately 20,000 protein-coding genes. Of these, dystrophin is the third largest; spanning ~2. Read More…
-
The quest to find the perfect gene therapy vector for the brain: in focus lysosomal storage disorders with neurological symptoms
As highlighted by Dr Stuart Nicklin’s post in April this year, scientists are working on developing new, more powerful adeno-associated vectors (AAV Read More…
-
Science Writing Competition
To recognise outstanding written communication by students (post-graduate and undergraduate) and research scientists (pre- and post-doc Read More…
-
Viruses, BiTEs, and T-cells: A Triple Threat to Tackle Cancer
A team of scientists from Barcelona (IDIBELL-Institut Català d’Oncologia) and Philadelphia (Perelman School of Medicine) combined three of the Read More…
-
Celebrating the path of research that led to today’s ground-breaking cell and gene therapies
As scientists from around the world descended on London last month to discuss monumental advances in gene and cell therapy research at the BSGCT Sprin Read More…
-
New Breakthrough in Stem Cell Therapy for Age-related Macular Degeneration
A team of scientists based primarily at Moorfields Eye Hospital and University College London has performed a study implanting embryonic stem cell pat Read More…
-
ESGCT & BSGCT Spring School 2018
Wednesday 21/03/18
On a brilliantly sunny day in Pembroke College, I made my way around (not over) a perfectly mowed lawn towards the grand hall for b Read More… -
From genes to medicine: an engaging day!
Thursday 15th March 2018. A 4.45am alarm. Read More… -
Evolving novel AAV vectors for efficient intravascular delivery across the blood brain barrier
The central nervous system (CNS) is an important target for gene therapy for a range of diseases including Freidrich’s Ataxia, spinal muscular atrop Read More…